GIVI-MPC, a stem cell therapy for certain types of muscular dystrophy, has been granted orphan drug status for treating ...
Columnist Patrick Moeschen was given an incorrect diagnosis of Becker muscular dystrophy, years before learning he actually ...
Columnist Betty Vertin woke up Christmas Eve scared and anxious at the thought that her youngest son with DMD would soon be unable to walk.
In the past few weeks, as I’ve sat down at my laptop to write my columns, I’ve often wondered if readers think I’m crazy. One week my columns are full of positivity and gratitude for the things I’ve ...
A gene-editing therapy may correct a defect in the DYSF gene that drives a form of limb-girdle muscular dystrophy (LGMD), per ...
Columnist Shalom Lim saw elements of his own journey with DMD reflected in the Netflix documentary "The Remarkable Life of ...
Capricor's biologics license application for deramiocel (CAP-1002) is draws largely on the Phase 2 HOPE-2 trial and its ...
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