Modern prophylactic therapies for hereditary angioedema with C1 inhibitor deficiency (HAE-C1INH) have become increasingly prevalent in Hungary, paralleling global trends, and are proving both ...

Physical activity before or during pregnancy was not associated with negative maternal/neonatal outcomes; however, physical activity was not statistically significantly associated with positive ...

Once-daily treprostinil palmitil inhalation powder (TPIP) has demonstrated significant promise as a next-generation therapy for pulmonary arterial hypertension (PAH), according to positive topline ...

Amyloid transthyretin cardiomyopathy (ATTR-CM) is a progressive and life-threatening heart disease that can lead to increased ventricular wall thickness, restrictive cardiomyopathy, and heart failure.

Due to a high incidence of invasive fungal infections after treatment with first- and second-generation Bruton tyrosine kinase inhibitors (BTKis), researchers are emphasizing the importance of ...

Researchers from Iran presented the case of a patient with chronic inflammatory demyelinating polyneuropathy (CIDP) who underwent emergency umbilical herniorrhaphy and whose anesthesia was ...

The levels of sialylated N-glycans in the serum could be a novel biomarker in chronic inflammatory demyelinating polyneuropathy (CIDP), according to a new study published in the European Journal of ...

A CRISPR/Cas9-modified Janus kinase 2 (JAK2) V617F model may be useful to develop new therapies against myeloproliferative neoplasms (MPNs), showed a new study published in the International Journal ...

Global start-up activities associated with the randomized, placebo-controlled, double-blind, global phase 3 ALPHA-ORBIT trial of navenibart (STAR-0215) for the treatment of patients with hereditary ...

Thirty-nine patients participated in the study. A total of 7.7% of patients presented with a previous history of OID that was diagnosed at a different institution. About half of the patients presented ...

A case of copper deficiency peripheral neuropathy (CDPN) associated with Wilson disease (WD) was described recently in the journal Acta Neurologica Belgica. Although CDPN has been described and linked ...

A supratherapeutic dose of 1400 mg of vatiquinone is safe and well-tolerated in patients with Friedreich ataxia (FA), according to a new study published in the journal Clinical Pharmacology in Drug ...