Muscular Dystrophy News6h
GIVI-MPC named FDA orphan drug for treatment of Becker MD
GIVI-MPC, a stem cell therapy for certain types of muscular dystrophy, has been granted orphan drug status for treating ...
Muscular Dystrophy News1d
My original diagnosis was incorrect. Here’s why that’s important.
Columnist Patrick Moeschen was given an incorrect diagnosis of Becker muscular dystrophy, years before learning he actually ...
Muscular Dystrophy News5d
Gene-editing therapy for LGMD shows promise in mouse model
A gene-editing therapy may correct a defect in the DYSF gene that drives a form of limb-girdle muscular dystrophy (LGMD), per ...
Muscular Dystrophy News6d
How ‘The Remarkable Life of Ibelin’ moved me as a DMD survivor
Columnist Shalom Lim saw elements of his own journey with DMD reflected in the Netflix documentary "The Remarkable Life of ...
Muscular Dystrophy News4d
Waking up on Christmas Eve made me scared and anxious
The Christmas decorations are down and tucked into storage for another year. The house is clean, the counters are clear of the holiday sweets, and our routine is again in sync. However, this holiday ...
Muscular Dystrophy News7d
Application finalized for DMD cell therapy CAP-1002, now deramiocel
Capricor Therapeutics has completed its submission of a biologics license application (BLA) seeking U.S. approval of deramiocel, the company’s cell therapy for heart muscle disease in people with ...